希少疾患

Your partner in developing orphan drugs to build a better tomorrow for patients with rare disease

Expect accountable delivery for the lifetime of your study.

Work with a reliable partner that works with urgency and integrity.

Leverage our innovative approach to advance your rare disease study.

Inspired by patients and families living with a rare disease

Being diagnosed with a rare disease can feel overwhelming and isolating. We understand the power of connecting with the right care team and with others facing similar circumstances. That's why we strive to foster that feeling of community-connection and contribution-within our clinical studies.

We believe each unique challenge and complexity represents an opportunity to show our agility and value. Together, with the engagement and inclusion of patients, families, and the broader community, we're committed to helping advance new orphan drugs for rare diseases.

実績を積み重ねたパートナーを選ぶことが重要です。

ぜひご相談ください

過去 5 年間の実績

当社は、開発における CRO パートナーとして、バイオテクノロジー企業や製薬会社のお客様に選ばれています。また、開発の前例がない新しい分野や未知の分野への慎重なアプローチにも定評をいただいています。以下は、過去 5 年間に当社がサポートを提供した実績です。

877

All rare disease studies

624

Rare disease studies outside of oncology

233

Pediatric rare disease studies

血液学

神経科学

代謝性疾患

循環器

Expect more for your next rare disease trial

当社はパートナーとして、貴社チームの一員として貢献します：

Provide proven patient-centric solutions that improve your study’s visibility and credibility
Offer experience optimizing collaboration with advocacy groups
Help navigate regulatory hurdles and clinical complexities to accelerate programs
Support informed endpoint development for rare disease
Deliver innovative solutions for biomarker models, mobile health, natural history studies and virtual trials
Enable customized site support
Advance diversity in clinical trials and optimizing inclusion of marginalized communities
Leverage real-world, value-based evidence that helps determine pricing and sets market access strategies

Get the latest updates from our team.

ニュースやイベント、出版物の最新情報をご紹介します。

WHITE PAPER

Effective planning to address unmet needs in Prader-Willi Syndrome trials

Read the white paper

ARTICLE

Rare diseases: A spotlight on Gaucher disease research in India

Read the article

ARTICLE

Advancing rare disease clinical trials and orphan drug research: A focus on APAC and China

Read the article

ARTICLE

Clinical trials in rare disease

Read the article

複雑で斬新な臨床試験に向け、機敏なパートナーとして貢献します

Let our multidisciplinary experts put their insights and experience to work to advance your rare disease drug development program. 当社とともに、お客様の可能性を成功へと導き、まだ満たされていない差し迫った医療ニーズに一石を投じましょう。

当社の関連専門分野をご覧ください。

細胞療法・遺伝子治療薬小児科当社チーム（RAPT）